This new therapy involves an innovative two-step strategy: Precision gene delivery: Using specialized enhancers (short ...

In a groundbreaking advancement for families grappling with the challenges of Dravet syndrome, a rare and life-altering form ...

By replacing the defective gene associated with Dravet syndrome in mice, scientists successfully alleviated symptoms without ...

Scientists developed a promising gene replacement therapy for Dravet syndrome in mice. The therapy alleviated symptoms ...

Listed below are links to the GEN stories reference in this episode of Touching Base Gene Therapy Tested in Mice Offers New ...

New research from the University of Colorado Anschutz Medical Campus is the first to identify defects related to metabolism ...

Dravet Syndrome impacts 1 in about every 15,700 ... The Allen Institute in Seattle have created a new gene replacement therapy in mice that could lead to better treatments in humans.

New research from the University of Colorado Anschutz Medical Campus is the first to identify defects related to metabolism (how the body processes and uses energy) in lymphoblast cell lines (LCLs) ...

Gene therapy breakthrough offers hope for severe Dravet syndrome cases Glioma mutations more common in firefighters, study reveals Discovery of gene silencer offers hope for autosomal dominant ...

Get Instant Summarized Text (Gist) A novel gene therapy has been developed that alleviates symptoms of Dravet syndrome in mice without side effects. This therapy uses a two-step strategy ...