This new therapy involves an innovative two-step strategy: Precision gene delivery: Using specialized enhancers (short stretches of DNA that act like switches to control when and where a specific gene ...

In a groundbreaking advancement for families grappling with the challenges of Dravet syndrome, a rare and life-altering form of epilepsy, scientists have developed a new gene replacement therapy in ...

In a step forward for the treatment of Dravet syndrome, scientists have developed a gene replacement therapy in mice that shows promise for more effective treatments in humans. The study, published ...

By replacing the defective gene associated with Dravet syndrome in mice, scientists successfully alleviated symptoms without side effects.

Listed below are links to the GEN stories reference in this episode of Touching Base Gene Therapy Tested in Mice Offers New ...

SEATTLE, Wash. -- Scientists at the Allen Institute have made a major breakthrough in research for people living with Dravet Syndrome, which is a rare and debilitating form of epilepsy that starts ...

New research from the University of Colorado Anschutz Medical Campus is the first to identify defects related to metabolism (how the body processes and uses energy) in lymphoblast cell lines (LCLs) ...

In a groundbreaking advancement for families grappling with the challenges of Dravet syndrome, a rare and life-altering form of epilepsy, scientists have developed a new gene replacement therapy ...