CGT Global, a leading biotechnology company driving the development and delivery of innovative cell and gene therapies, today ...

US Food and Drug Administration Commissioner Marty Makary said he’s trying to persuade Vinay Prasad, the agency’s former head ...

Sarepta Therapeutics (NASDAQ:SRPT) has hired a lobbying firm with close ties to the Trump administration as regulatory ...

A 26-year-old Downriver man seen at Children’s Hospital of Michigan in Detroit since infancy for a rare bleeding disorder in ...

Currently, GenAns Biotech is conducting investigator-initiated trials for several gene therapies, including GA001 for ...

The Revell family hoped a gene therapy could buy time for their sons, who have a rare and fatal disease. After two patients ...

The primary safety risks associated with gene therapy include immune reactions and off-target effects in unintended organs, ...

Parents of boys with Duchenne muscular dystrophy weigh in on drug innovation and medical regulation.

Gene therapy has been headline news in recent years, in part due to the rapid development of biotechnology that enables doctors to administer such treatments. Broadly, gene therapies are ...

Gene therapy appears to be a promising approach for a subset of genetic deafness, although challenges remain with development ...

Leveraging Northway Biotech’s 20+ years of CDMO expertise, Diorasis Therapeutics is advancing AAV gene therapy for glaucoma ...

Choosing gene therapy Gray was in and out of hospitals seven times during each of the two years before her gene therapy. Then 32, she explained to her doctor that she was too tired to go on.