The SMA gene therapy candidate OAV101 IT, a version of Zolgensma, can be safely given to previously treated patients, per new ...

Thanks to the 21st Century Cures Act, columnist Brianna Albers tends to needlessly stress about lab results her doctor hasn't yet reviewed.

This weekend kicked off the MDA annual Clinical & Scientific Conference, bringing together the neuromuscular disease ...

SMA patients want PROMs that focus on more than physical function, and that also assess mental health, sexual function, sleep ...

Winters are hard for columnist Alyssa Silva — as is life with SMA. She reminds herself of the importance of finding light in ...

A study based on a survey of 50 adults linked poorer quality sleep with more depressive symptoms and respiratory issues in ...

Hurricane Helene and recent storms have taken a toll on the tree that stands guard over columnist Helen Baldwin's late son's resting spot.

The three diagnostic tests for identifying genetic mutations associated with SMA met new European Union regulatory ...

Disease-modifying therapies (DMTs) may help lower the risk of children's bone fractures in spinal muscular atrophy (SMA), a ...