Rheumatology Advisor4h
Apitegromab Gets Priority Review for Spinal Muscular Atrophy
The FDA has accepted for Priority Review the BLA for apitegromab for the improvement of motor function in patients with spinal muscular atrophy.
Film on boy's rare disability nominated for Bafta
A film about a Kent boy who lives with a rare condition has been nominated for a Bafta TV award. Sky's Disability & Me ...
Irish Medical Times9h
Two years on, promised new conditions yet to be added to newborn ‘heel prick’ test
Survey finds that 59 per cent of those planning a family have concerns about the slow pace of newborn screening expansion ...