The arc of biotechnology is one of breakthroughs and struggles, writes Tim Hunt, CEO of the Alliance for Regenerative ...

Sarepta Therapeutics announced that a patient with Duchenne muscular dystrophy who received Elevidys (delandistrogene moxeparvovec-rokl) died following treatment.

This approval was followed by Takeda Pharmaceuticals’ Alofisel (darvadstrocel), which received approval from the European Medicines Agency in 2018 and from Japan’s Pharmaceuticals and Medical Devices ...

Medical history has recently been made in a New York City hospital. This month, 21-year-old Sebastien Beauzile became the ...

The biotechnology sector has experienced a jolt of volatility over the past few days, spearheaded by the dramatic price ...

Hubble Therapeutics LLC a patient-focused biotechnology company developing a gene therapy to cure pediatric blindness, announces the successful ...

Verve received FDA IND clearance for VERVE-102 to treat HeFH, adding new trial sites in the United States. Read more about ...

Learn how to navigate cystic fibrosis care with confidence, from treatments and school plans to building a supportive medical ...

Charles C. Wykoff, MD, PhD, Retinal Consultants of Texas, discusses data supporting the FDA approval of revakinagene taroretcel-lwey (Encelto; Neurotech Pharmaceuticals), the first and only therapy ...

The aggregate gross proceeds to Benitec from the underwritten offering and the concurrent registered direct offering are expected to be approximately $30 million, prior to deducting underwriting ...

Tonix Pharma (TNXP) has submitted an NDA for its candidate TNX-102 SL for fibromyalgia, with a PDUFA date set for August 15, ...

Bank of New York Mellon Corp lessened its holdings in Voyager Therapeutics, Inc. (NASDAQ:VYGR – Free Report) by 22.5% in the 4th quarter, according to its most recent filing with the SEC. The firm ...