Intrathecal treatment with a vector-based gene therapy was associated with a greater improvement in motor function at 52 ...

The FDA has accepted for Priority Review the BLA for apitegromab for the improvement of motor function in patients with spinal muscular atrophy.

Leader of Opposition Suvendu Adhikari donated Rs 10 lakh from his salary towards the treatment of a girl from West Bengal's ...

A film about a Kent boy who lives with a rare condition has been nominated for a Bafta TV award. Sky's Disability & Me ...

The bench said that public good outweighs the company’s profit as the drug is not available at an affordable price in India.

“During the wait for the results, things deteriorated. He was choking constantly, not going to the toilet for days and his ...

Japanese drugmaker Chugai (TYO: 4519) has obtained regulatory approval from the Ministry of Health, Labor and Welfare (MHLW) ...

Chugai Pharma’s Evrysdi tablets 5mg receives Japanese approval to treat spinal muscular atrophy: Saturday, March 29, 2025, 11:00 Hrs [IST] Chugai Pharmaceutical Co., Ltd. announ ...

PTC Therapeutics, Inc. (NASDAQ:PTCT – Get Free Report)’s share price dropped 8.8% during trading on Monday after JPMorgan ...

Survey finds that 59 per cent of those planning a family have concerns about the slow pace of newborn screening expansion ...